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Carmen Leon Astudillo, MD

Pediatric Neuromuscular Rehabilitation Specialist, Pediatric Pulmonologist (Child Lung Specialist)

Photo of Carmen Leon Astudillo
(352) 265-8250 MyUFHealth

Research at a glance

Top areas of exploration

  • Genetic Therapy , 2 publications
  • Sleep Apnea, Obstructive , 2 publications
  • Pediatrics , 2 publications
  • Immunoglobulins, Intravenous , 2 publications

Research activity

23 publications

232 citations

Why is this important?

Active clinical trials

SRP-9001-305 EXPEDITION

The purpose of this study is to provide a single clinical study with a uniform approach to monitoring long-term safety and efficacy in participants who received delandistrogene moxeparvovec in a previous clinical study. No study drug will be…

Investigator
Carmen Leon Astudillo
Status
Accepting Candidates
Ages
N/A - N/A
Sexes
Male
BN44620

This is an open-label, single-arm, multicenter clinical study to evaluate the effectiveness and safety of risdiplam administered as an early intervention in pediatric participants with spinal muscular atrophy (SMA) and 2 SMN2 copies who have…

Investigator
Carmen Leon Astudillo
Status
Accepting Candidates
Ages
3 Months - 24 Months
Sexes
All
9001-303 (ENVISION)

The study will evaluate the safety and efficacy of delandistrogene moxeparvovec gene transfer therapy in non-ambulatory and ambulatory males with DMD. This is a randomized, double-blind, placebo-controlled 2-part study. Participants will be in the…

Investigator
Carmen Leon Astudillo
Status
Accepting Candidates
Ages
N/A - N/A
Sexes
Male

My publications

Filter publications

23 publications

2024

Twelve Tips to Succeed as Health Profession Clinical Educator in Resource-Limited Settings

Advances in Medical Education and Practice

Publisher's site

2024

Longitudinal changes of swallowing safety and efficiency in infants with spinal muscular atrophy who received disease modifying therapies

Pediatric Pulmonology

Publisher's site

2024

Thrombotic microangiopathy following systemic AAV administration is dependent on anti-capsid antibodies.

The Journal of clinical investigation

PubMed • Publisher's site

2023

Sensitivity of Pharmacokinetics to Differences in the Particle Size Distribution for Formulations of Locally Acting Mometasone Furoate Suspension-Based Nasal Sprays.

Molecular pharmaceutics

PubMed • Publisher's site