Efficacy of Medication in Adults With Friedreich Ataxia

Purpose

The purpose of this study is to evaluate the efficacy of a study drug on arms and hands motor function and manual dexterity. It is also to evaluate the drug on various neurological functions, safety, and tolerability.

Procedures

  • The study involves approximately 6 visits over 3 months
  • Participants will take a study medication or a placebo
  • Visits will include questionnaires, an electrocardiogram (ECG), medical exams, blood and urine tests, movement tests

Eligibility

  • 18-55 years old
  • Diagnosed with Freidreich's Ataxia
  • BMI between 16 and 40

Age

18 to 65

Gender

Male
Female

Monetary compensation

No

Keywords

Friedreich's ataxia, Ataxia, Friedreich ataxia, Spinocerebellar degeneration, Central nervous system

Principal Investigator

S.H. Subramony, MD

Department

Department of Neurology

Contact Information

rebecca.dettorre@neurology.ufl.edu

(352) 294-8948


Be an Informed Participant

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Know Who to Contact

  • Eligibility: For questions about a specific study and who is eligible to participate, call or email the contact person listed for that study.
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