All results

3 results for progress phase i and open label randomized controlled phase ii study testing safety

• Conditioning SCID Infants Diagnosed Early (CSIDE)

  The investigators want to study if lower doses of chemotherapy will help babies with SCID to achieve good immunity with less short and long-term risks of…

  Ages

  0 Years - 2 Years

  Sexes

  All

• ALXN2050-NEPH-201

  This is a Phase 2, randomized, double-blind, placebo-controlled, multicenter study of ALXN2050 (120 and 180 milligrams [mg]) in addition to background therapy…

  Ages

  18 Years - 75 Years

  Sexes

  All

• BOSTON 3

  The objective of the trial is to assess the long-term safety and efficacy of L-CsA plus Standard of Care (SoC) in the treatment of BOS in single (SLT) and…

  Ages

  18 Years - N/A

  Sexes

  All