All results

13 results

• Palekona-GS-US-457-6411

  The goal of this study is to learn if tilpisertib fosmecarbil (formerly known as GS-5290) is effective and safe in treating participants with moderate to…

  Ages

  18 Years - 75 Years

  Sexes

  All

• Safety and Efficacy of NMD670 in Ambulatory Adult Patients With Type 3 Spinal Muscular Atrophy

  The purpose of this study is to evaluate the efficacy, safety, tolerability and pharmacokinetics of NMD670 in the treatment of ambulatory adults with spinal…

  Ages

  18 Years - 75 Years

  Sexes

  All

• Takeda TAK-999-3001

  The main aim of this study is to learn if fazirsiran reduces liver scarring (fibrosis) compared to placebo. Other aims are to learn if fazirsiran slows down…

  Ages

  18 Years - 75 Years

  Sexes

  All