All results
530 results
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1305-0014 (FIBRONEERTM IPF)
This study is open to adults with a lung disease called Idiopathic Pulmonary Fibrosis (IPF). People can join the study if they are 40 years or older. If they…
- Ages
- 40 Years - N/A
- Sexes
- All
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1305-0023 (FIBRONEERTM ILD)
This study is open to adults with Progressive Fibrosing Interstitial Lung Diseases (PF-ILDs). People who have a form of PF-ILD other than Idiopathic Pulmonary…
- Ages
- 18 Years - N/A
- Sexes
- All
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1Florida ADRC
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307-201 - Gene Therapy
This is a Phase 1/2, open-label, dose escalation study to evaluate the safety, efficacy and tolerability of BMN 307 in adult PKU subjects with PAH deficiency.…
- Ages
- 15 Years - N/A
- Sexes
- All
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4045-302
The main objective of this study is to evaluate the safety and tolerability of long-term treatment with casimersen or golodirsen in patients with Duchenne…
- Ages
- 7 Years - 23 Years
- Sexes
- Male
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5-Fluorouracil, Oxaliplatin + Dasatinib(FolFox-D) in First-Line Metastatic Pancreatic Adenocarcinoma
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7089 PAL-LIVER
This is a comparative effectiveness study of two pragmatic models aiming to introduce palliative care for end stage liver disease patients. The 2 comparators…
- Ages
- 18 Years - 120 Years
- Sexes
- All
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9001-303 (ENVISION)
The study will evaluate the safety and efficacy of delandistrogene moxeparvovec gene transfer therapy in non-ambulatory and ambulatory males with DMD. This is…
- Ages
- N/A - N/A
- Sexes
- Male
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A 5-year Longitudinal Observational Study of Patients With NAFL or NASH
TARGET-NASH is a longitudinal observational cohort study of patients being managed for NASH and related conditions across the entire spectrum NAFLD in usual…
- Ages
- 2 Years - N/A
- Sexes
- All
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A Clinical Trial of 3 Doses of PRAX-944 in Participants With Essential Tremor
This multi-center, randomized, double-blinded, placebo-controlled, dose-range-finding clinical trial (with an optional Extension comprised of an Extension…
- Ages
- 18 Years - N/A
- Sexes
- All