All results

2 results for randomized double blind multiple dose placebo controlled study evaluate safety

• EMBARK

  The study will evaluate the safety and efficacy of gene transfer therapy in boys with DMD. It is a randomized, double-blind, placebo-controlled study. The…

  Ages

  4 Years - 7 Years

  Sexes

  Male

• Edgewise-210

  The LYNX study is a 2-part, multicenter, Phase 2 study of safety, pharmacokinetics and biomarkers in children with Duchenne muscular dystrophy including a…

  Ages

  4 Years - 9 Years

  Sexes

  Male