All results
3 results for randomized double blind placebo controlled study assess efficacy safety and
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Edgewise-201 (CANYON)
A study of EDG-5506 in Becker muscular dystrophy (known as CANYON) and pivotal cohort (known as GRAND CANYON). The EDG-5506-201 CANYON study was expanded to…
- Ages
- 12 Years - 50 Years
- Sexes
- Male
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9001-303 (ENVISION)
The study will evaluate the safety and efficacy of delandistrogene moxeparvovec gene transfer therapy in non-ambulatory and ambulatory males with DMD. This is…
- Ages
- N/A - N/A
- Sexes
- Male
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EMBARK
The study will evaluate the safety and efficacy of gene transfer therapy in boys with DMD. It is a randomized, double-blind, placebo-controlled study. The…
- Ages
- 4 Years - 7 Years
- Sexes
- Male