All results
33 results for randomized double blind placebo controlled study assess efficacy safety and
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9001-303 (ENVISION)
The study will evaluate the safety and efficacy of delandistrogene moxeparvovec gene transfer therapy in non-ambulatory and ambulatory males with DMD. This is…
- Ages
- N/A - N/A
- Sexes
- Male
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ATYR
This randomized, double-blind, placebo matched to efzofitimod-controlled, study will evaluate the safety, tolerability, immunogenicity, pharmacokinetic (PK),…
- Ages
- 18 Years - 75 Years
- Sexes
- All
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Adaptive COVID-19 Treatment Trial (ACTT)
This study is an adaptive, randomized, double-blind, placebo-controlled trial to evaluate the safety and efficacy of novel therapeutic agents in hospitalized…
- Ages
- 18 Years - 99 Years
- Sexes
- All
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Armata
Phase 1b/2a, Randomized, Double-Blind, Placebo-Controlled, Multiple Ascending Dose Escalation Study of the Safety, Tolerability, and Efficacy of Intravenous AP…
- Ages
- 18 Years - N/A
- Sexes
- All
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Atacicept in Subjects With IgA Nephropathy
A Phase 3 Study with Atacicept in Subjects With IgA Nephropathy (ORIGIN 3) This is a multi-part study comprising of the original Phase 2b study (active, no…
- Ages
- 18 Years - N/A
- Sexes
- All
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BOOST3
BOOST3 is a randomized clinical trial to determine the comparative effectiveness of two strategies for monitoring and treating patients with traumatic brain…
- Ages
- 14 Years - N/A
- Sexes
- All
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CC-90001 in Subjects With Idiopathic Pulmonary Fibrosis
This is a Phase 2, multicenter, multinational, randomized, double-blind, placebo-controlled study evaluating the efficacy, safety, pharmacokinetics (PK),…
- Ages
- 40 Years - N/A
- Sexes
- All
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CTD-TCNPC-301
A prospective, randomized, double-blind, placebo controlled, multi-center therapeutic study for patients age 3 and older with confirmed diagnosis of Niemann…
- Ages
- 3 Years - N/A
- Sexes
- All
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EMBARK
The study will evaluate the safety and efficacy of gene transfer therapy in boys with DMD. It is a randomized, double-blind, placebo-controlled study. The…
- Ages
- 4 Years - 7 Years
- Sexes
- Male
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Edgewise-201 (CANYON)
A study of EDG-5506 in Becker muscular dystrophy (known as CANYON) and pivotal cohort (known as GRAND CANYON). The EDG-5506-201 CANYON study was expanded to…
- Ages
- 12 Years - 50 Years
- Sexes
- Male